A PHASE IIA MULTICENTER, OPEN-LABEL, 12-WEEK STUDY TO INVESTIGATE THE PHARMACOKINETICS AND SAFETY AND TO PROVIDE PROOF OFMECHANISM OF ALOGABAT IN CHILDREN AND ADOLESCENTS AGED 517 YEARS WITH ANGELMAN SYNDROME (AS) WITH DELETION GENOTYPE
Sponsor: |
F. Hoffman La Roche Ltd |
Enrolling: |
Male and Female Patients |
IRB Number: |
AAAU5011 |
Contact: |
Jennifer Bain: / jb3634@cumc.columbia.edu |
This is a Phase IIA Multicenter, open-label, 12-week study to investigate the pharmacokinetics and safety and to provide proof of mechanism of the drug, Alogabat (RO7017773) in children and adolescents aged 5-17 years old with Angelman Syndrome with the deletion genotype.
Investigator
Jennifer Bain, MD
Is your child between 5-17 years old? |
Yes |
No |
Has your child been diagnosed with Angelman Syndrome (AS)? |
Yes |
No |