Downsyndrome (DS) occurs in roughly 1 out of 700 births in the U.S. Half of all children with Downsyndrome have congenital heart disease (CHD), often requiring corrective heart surgery. Even though CHD in children without DS is known…
This study is for patients with Lambert-Eaton Myasthenic Syndrome (LEMS). The purpose of this study is to provide doctors and their patients access to amifampridine phosphate therapy for their patients with LEMS, CMS or downbeat nystagmus until the product becomes commercially available. The…